Materials
Session I: Introductions & Project Overview
Welcome & Introductions
Veronica Miller, Forum
José-Alain Sahel, UPMC Vision Institute
Daniel Chung, SparingVision
Governance & Forum Process
Sehyr Khan, Forum
Alessi Ayvaz, Forum
Objectives for Ocular Diseases Forum 3 (ODF3)
Claire M. Gelfman, Forum
Session II: Ongoing Collaborations and Current Efforts
Ongoing Efforts: ERN-EYE
Bart Leroy, Ghent University
Regulatory Endpoints and Trial Design for IRDs (REDI) Working Group: Ongoing Efforts
Rachel Huckfeldt, Massachusetts Eye and Ear
Session III: Full-field Stimulus Testing (FST) for Consideration as an Endpoint
Overview: Endpoints Working Group
Sehyr Khan, Forum
Overview of Full-field Stimulus Testing (FST)
Artur Cideciyan, University of Pennsylvania*
Clinical Trial Data Presentation #1 (Spark)
Daniel Chung, SparingVision
Full-field Stimulus Test (FST) as a Clinical Endpoints in a Phase 1/2 Study of ATSN-101
Laura Pardon, Atsena Therapeutics
Recovery of Cone-Mediated Vision in a Severe Ciliopathy after Gene Augmentation: One Year Results of a Phase Ib/IIa Trial for LCA5-LCA
Tomas Aleman, University of Pennsylvania*
FST Minimal Clinically Important Difference
Lee McDaniel, Jaeb Center for Health Research
Session IV: Endpoints Working Group: Defining the Patient Population for FST
Considerations for Clinical Trial Population for FST
Rachel Huckfeldt, Massachusetts Eye and Ear
Session V: Endpoints Working Group: Looking Towards the Future
Patient Perspective: Fireside Chat
Matthew Baier
Ned Reade, BCM Families Foundation
Barbara Wade Sergent, BCM Families Foundation
Outcome measures in IRDS: Focus on PBTs
José-Alain Sahel, UPMC Vision Institute
Patient-Reported Outcome Measures in IRDs: Informing a Consensus Statement
Todd Durham, Foundation Fighting Blindness
Session VI: Endpoints Working Group: Considerations for Age-Related Macular Degeneration (AMD)
Current Landscape for iAMD Drug Development
Cheryl Rowe-Rendleman, Omar Consultants
Session VII: Wrap Up & Next Steps
Closing Panel
Daniel Chung, SparingVision
Veronica Miller, Forum
José-Alain Sahel, UPMC Vision Institute